Detalhe da pesquisa
1.
Improved efficacy of FKRP AAV gene therapy by combination with ribitol treatment for LGMD2I.
Mol Ther
; 31(12): 3478-3489, 2023 Dec 06.
Artigo
em Inglês
| MEDLINE | ID: mdl-37919902
2.
Ribitol dose-dependently enhances matriglycan expression and improves muscle function with prolonged life span in limb girdle muscular dystrophy 2I mouse model.
PLoS One
; 17(12): e0278482, 2022.
Artigo
em Inglês
| MEDLINE | ID: mdl-36454905